Table 3 Impact of the home-based infusions on Treatment Satisfaction in Enrolled population
Cohort A (N = 32) n (%) | Cohort B (N = 6) n (%) | Total (N = 38) n (%) | |
|---|---|---|---|
Number of patients who completed the home infusion satisfaction questionnaire at screening | 32 (100.00) | 6 (100.00) | 38 (100.00) |
Where do you prefer to take your ERT infusions? | |||
Hospital/clinic near your home | 1 (3.13) | 0 | 1 (2.63) |
Home | 31 (96.88) | 6 (100.00) | 37 (97.37) |
Why do you prefer to take your ERT infusion in home setting? a | |||
More convenient | 26 (81.25) | 5 (83.33) | 31 (81.58) |
Less stressful | 20 (62.50) | 3 (50.00) | 23 (60.53) |
Daily activities are less disrupted | 14 (43.75) | 2 (33.33) | 16 (42.11) |
Work/school are less disrupted | 8 (25.00) | 3 (50.00) | 11 (28.95) |
Family life is less disrupted | 8 (25.00) | 3 (50.00) | 11 (28.95) |
Less transportation needed (drive, take bus/taxi/train) | 21 (65.63) | 3 (50.00) | 24 (63.16) |
More clinical supervision | 3 (9.38) | 1 (16.67) | 4 (10.53) |
Feel less socially isolated | 1 (3.13) | 1 (16.67) | 2 (5.26) |
Other | 2 (6.25) | 0 | 2 (5.26) |
In general, and despite your LSD, would you say your health is: | |||
Excellent | 2 (6.25) | 0 | 2 (5.26) |
Very good | 5 (15.63) | 1 (16.67) | 6 (15.79) |
Good | 16 (50.00) | 5 (83.33) | 21 (55.26) |
Fair | 4 (12.50) | 0 | 4 (10.53) |
Poor | 5 (15.63) | 0 | 5 (13.16) |
If you are receiving ERT at home, how would you rate health in general compared to the period you received ERT in the hospital? | |||
Much better now | 6 (18.75) | 3 (50.00) | 9 (23.68) |
Somewhat better now | 6 (18.75) | 2 (33.33) | 8 (21.05) |
About the same | 19 (59.38) | 1 (16.67) | 20 (52.63) |
Missing | 1 (3.13) | 0 | 1 (2.63) |